Gene therapy poses one of the greatest technical challenges in modern medicine. It is very hard to introduce new genes into cells of the body and keep them working.

Jun 17, 2025 · However, gene therapy also faces significant challenges, including off-target effects, immune responses, and high costs. In this article, we will explore the current trends and challenges …

Jul 1, 2025 · In addition to their expense, an additional roadblock for access to cell and gene therapies is that they have complex treatment pathways and require specialised centres for their delivery.

Jun 6, 2025 · Over 100 rare disease gene therapies have been discontinued not due to treatment failure, but market viability concerns. FDA officials, including Commissioner Martin Makary and top …

Jul 24, 2025 · Gene therapy has traditionally focused on rare, single gene (monogenic) disorders. Sanofi is now building on these innovations to tackle more common immune-mediated diseases including …

Dec 25, 2024 · Conclusion: The state of cell and gene therapy is evolving rapidly, with groundbreaking therapies coming to market and ongoing clinical research expanding treatment possibilities. …

Feb 3, 2025 · To benchmark the sector’s progress in our inaugural print issue of Cell & Gene Therapy Review, we asked thought leaders a single question: What is the biggest challenge facing the CGT …

Apr 2, 2024 · This article explores the complexities and challenges of gene therapy, revealing the hurdles that scientists and medical professionals face in turning theoretical cures into tangible realities.

Mar 31, 2025 · This report provides a comprehensive overview of gene therapy, encompassing various gene editing technologies, delivery strategies, target diseases, associated challenges, ethical …

May 5, 2025 · Gene therapy holds the promise to revolutionize medicine by providing cures for previously untreatable genetic disorders. However, the path from discovery to commercialization is …